Scientists have created a new therapeutic approach for testing fragile X syndrome, which is the most common genetic cause of autism spectrum disorder (ASD). This method aims to alter a type of neural ...

After its cannabidiol gel candidate failed a phase 3 trial in fragile X syndrome, Harmony Biosciences has now paused development of the asset in a different genetic disease. Harmony announced in ...

When it came time to start a family, Sarah Elizabeth Orlando, 33, knew she would go about it differently. Before she was born, an in-utero amniocentesis had confirmed she carried the gene for fragile ...

New research has identified a potential method for treating fragile X syndrome, a leading cause of autism spectrum disorders that is characterized by an inherited repeat of certain nucleotides within ...

An experimental drug appears to help people with a genetic disorder called Fragile X syndrome. Fragile X is the most common inherited cause of intellectual disabilities and autism. NPR's Jon Hamilton ...

Servier acquires KER-0193, a potential treatment for Fragile X syndrome, developed by Kaerus Bioscience, a Medicxi company KER-0193, a novel, orally bioavailable small molecule, was granted Orphan ...

"Hearst Magazines and Yahoo may earn commission or revenue on some items through these links." When it came time to start a family, Sarah Elizabeth Orlando, 33, knew she would go about it differently.